The FDA has asked Sarepta to reveal results of muscle biopsies to see how much new dystrophin was made after treatment with eteplirsen, but haven’t they already said studies only showed 0.9% increase? Will this new release provide any new information and give hope to Sarepta investors, not to mention patients and families, or is […]
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Sarepta and dystrophin
Sinclair Lewis wrote Arrowsmith in 1925 which discussed a fictional phage treatment for plague. Does fiction precede reality? Rob P.[...]